Aflac ST1001 Prolonged Isotretinoin

Tivantinib in Treating Younger Patients With Relapsed or Refractory Solid Tumors

CBCT for Parents of Children With Autism

Bone Marrow Transplantation vs Standard of Care in Patients With Severe Sickle Cell Disease (BMT CTN 1503)

A Study of Nivolumab Plus Brentuximab Vedotin in Patients Between 5 and 30 Years Old, With Hodgkin's Lymphoma (cHL), Relapsed or Refractory From First Line Treatment

Anti-LPS Antibody Treatment for Pediatric NAFLD

Mechanisms of Active Music Engagement to Improve Health Outcomes of Children With Cancer and Parents

MRI to Characterize and Predict CF Liver Disease in PUSH Cohort

Pumps for Kids, Infants, and Neonates

Abatacept for GVHD Prophylaxis After Hematopoietic Stem Cell Transplantation for Pediatric Sickle Cell Disease

Gabapentin Premedication for ACL Reconstruction: RCT

Effect of Ketorolac on Post Adenotonsillectomy Pain

Immune Monitoring and Assay Development in Organ Transplant Recipients

Longitudinal Study of Mitochondrial Hepatopathies

Study to Evaluate a Single Dose of Apixaban in Pediatric Subjects at Risk for a Thrombotic Disorder

AMD3100 for Sensitizing in Allogeneic Blood or Marrow Transplant for Chemotherapy Resistant Pediatric Acute Leukemia

Phase II Pegylated Interferon

Efficacy Study Of Tofacitinib In Pediatric JIA Population

A 5-year Longitudinal Observational Study of Patients With Nonalcoholic Fatty Liver (NAFL) or Nonalcoholic Steatohepatitis (NASH)

National Collaborative to Improve Care of Children With Complex Congenital Heart Disease

Randomized Controlled Trial of Valganciclovir for Cytomegalovirus Infected Hearing Impaired Infants

AflacLL1602 ENCERT

Evaluation of Fontan-Associated Liver Disease

A Study to Assess the Safety, Tolerability, and Efficacy of ST-400 for Treatment of Transfusion-Dependent Beta-thalassemia (TDT)

Study of Dose Confirmation and Safety of Crizanlizumab in Pediatric Sickle Cell Disease Patients

Acceptability, Feasibility and Safety of a Yoga Program for Chronic Pain in Sickle Cell Disease

Analysis of T-Cell Immune Reconstitution Following Allogeneic Hematopoietic BMT for Severe SCD

Evaluating the Genetic Causes and Progression of Cholestatic Liver Diseases (LOGIC)

Temozolomide, Cixutumumab, and Combination Chemotherapy in Treating Patients With Metastatic Rhabdomyosarcoma

Home Away From Home - Medical Outcomes

A Phase 1 Study of the EZH2 Inhibitor Tazemetostat in Pediatric Subjects With Relapsed or Refractory INI1-Negative Tumors or Synovial Sarcoma

Matched Targeted Therapy For High-Risk Leukemias and MDS

Urological and Renal Disease Engaging Adolescents in Adherence Collaborative Trial

Study Comparing Efficacy and Safety of Defibrotide vs Best Supportive Care in the Prevention of Hepatic Veno-Occlusive Disease in Adult and Pediatric Patients

Phase I Study of APX005M in Pediatric CNS Tumors

Safety, Tolerability, Efficacy and Pharmacokinetics of Copanlisib in Pediatric Patients

Rifaximin for Infection Prophylaxis in Hematopoietic Stem Cell Transplantation

Gabapentin Premedication to Reduce Postoperative Pain for Pediatric Tonsillectomy

Ribociclib in Combination With Everolimus and Dexamethasone in Relapsed ALL

Alpha-Defensin and Synovial Proteins to Improve Detection of Pediatric Septic Arthritis

Phase I/II Study of MEK162 for Children With Ras/Raf Pathway Activated Tumors

Closure of Muscular Ventricular Septal Defects (VSDs) With the AMPLATZER Muscular VSD (MuVSD) Occluder - Post Approval Study

A Multicenter Access and Distribution Protocol for Unlicensed Cryopreserved Cord Blood Units (CBUs)

Study of IDO Inhibitor and Temozolomide for Adult Patients With Primary Malignant Brain Tumors

Safety Study of Unlicensed, Investigational Cord Blood Units Manufactured by the NCBP for Unrelated Transplantation

Pediatric Obesity Weight Evaluation Registry (POWER) Study

Long-Term Safety Study Of Tofacinib In Patients With Juvenile Idiopathic Arthritis

Deflazacort Expanded Access Program for Children, Adolescents and Adults With Duchenne Muscular Dystrophy

Amifampridine Phosphate for the Treatment of Congenital Myasthenic Syndromes

MRI Markers of Outcome After Severe Pediatric TBI

A Extension Study of Udenafil in Adolescents

Pediatric ACL: Understanding Treatment Options

STRIDE Biorepository

MyHeartBaby: An Initial Evaluation of the MyHeartBaby Psychosocial Telemedicine Program

HeadStart4: Newly Diagnosed Children (

Dalbavancin for the Treatment of Acute Bacterial Skin and Skin Structure Infections in Children, Known or Suspected to be Caused by Susceptible Gram-positive Organisms, Including MRSA

Xeltis Bioabsorbable Pulmonary Valved Conduit Early Feasibility Study

Pharmacokinetics and Pharmacodynamics Study of SEG101 (Crizanlizumab) in Sickle Cell Disease (SCD) Patients With Vaso- Occlusive Crisis (VOC)

Intranasal Dexmedetomidine Sedation in Children for Non-painful Procedures

Stress Hydrocortisone In Pediatric Septic Shock

Pharmacokinetics of Anti-epileptic Drugs in Obese Children

Ribociclib and Everolimus in Treating Children With Recurrent or Refractory Malignant Brain Tumors

Improving Health-Promoting Behaviors in Adolescent Cancer Survivors Using AWAKE: A Feasibility Trial

Congenital Heart Disease Research Registry

Bortezomib and Combination Chemotherapy in Treating Young Patients With Relapsed Acute Lymphoblastic Leukemia or Lymphoblastic Lymphoma

Study of Sirolimus With PEG-Asparaginase in Acute Lymphoblastic Leukemia (ALL)

Rifaximin for Preventing Acute Graft Versus Host Disease (AGVHD)

Surgical Planning for Reconstruction of Complex Heart Defects

A Study To Find Out How Fesoterodine Works In Children Aged 6 To 17 Years With Bladder Overactivity Caused By A Neurological Condition

Long-term Follow-up of HLH Patients Who Received Treatment With NI-0501, an Anti-interferon Gamma Monoclonal Antibody

A Study Evaluating the Safety and Efficacy of the LentiGlobin BB305 Drug Product in Severe Sickle Cell Disease

Phase 2 Study of Alisertib Therapy for Rhabdoid Tumors

Patient Centered Comprehensive Medication Adherence Management System in Patients With Sickle Cell Disease

Safety Study of Gene Modified Donor T-cells Following TCR Alpha Beta Depleted Stem Cell Transplant

Efficacy and Safety of Rivipansel (GMI-1070) in the Treatment of Vaso-Occlusive Crisis in Hospitalized Subjects With Sickle Cell Disease

Dasatinib in Combination With Chemotherapy for Relapsed or Refractory Core Binding Factor Acute Myeloid Leukemia

Transplantation Using Reduced Intensity Approach for Patients With Sickle Cell Disease From Mismatched Family Donors of Bone Marrow

A Study of the Safety and Pharmacokinetics of Apixaban Versus Vitamin K Antagonist (VKA) or Low Molecular Weight Heparin (LMWH) in Pediatric Subjects With Congenital or Acquired Heart Disease Requiring Anticoagulation

Home Away From Home - Quality of Life Surveys

Crizotinib (Xalkori) Expanded Access Protocol For The Treatment Of Adult Or Pediatric Patients

Longitudinal Assessment of Transient Elastography in Cystic Fibrosis

Study of Gene Modified Donor T-cells Following TCR Alpha Beta Positive Depleted Stem Cell Transplant

Neuroblastoma Precision Trial

Study of Lorlatinib (PF-06463922)

Study to Assess Safety and Preliminary Activity of Eribulin Mesylate in Pediatric Participants With Relapsed/Refractory Rhabdomyosarcoma (RMS), Non-rhabdomyosarcoma Soft Tissue Sarcoma (NRSTS) and Ewing Sarcoma (EWS)

Efficacy of a Decision Aid for Hydroxyurea in Sickle Cell Disease

Music Therapy With Intubated and Sedated Pediatric Patients

Evaluating the Effects of Propofol vs. Dexmedetomidine

Universal Screening for Vocal Fold Motion Impairment in Children Undergoing Congenital Cardiac Surgery

Three Times Weekly (TIW) Growth Hormone Therapy in Children on Hemodialysis

Non-invasive Vagus Nerve Stimulation (nVNS) in Pediatric Chronic Inflammatory Demyelinating Polyneuropathy (CIDP)

Naive T Cell Depletion for Preventing Chronic Graft-versus-Host Disease in Children and Young Adults With Blood Cancers Undergoing Donor Stem Cell Transplant

Extension Study of AG-348 in Adult Participants With Pyruvate Kinase Deficiency Previously Enrolled in AG-348-006 or AG348-C-007

Gabapentin and Chronic Post Surgical Pain