An Intermediate Access Protocol for Selumetinib for Treatment of Neurofibromatosis Type 1

Caffeine and Neurologic Recovery Following Surgery and General Anesthesia

Ponatinib in Participants With Resistant Chronic Phase Chronic Myeloid Leukemia (CP-CML) to Characterize the Efficacy and Safety of a Range of Doses

Assessment of INS1007 in Subjects With Non-Cystic Fibrosis Bronchiectasis

Feasibility of Immediate Postpartum Long-acting Reversible Contraception Implementation

Trial to Evaluate Efficacy and Safety of Lenabasum in Diffuse Cutaneous Systemic Sclerosis

A Phase 2 Study of Mavacamten in Adults With Symptomatic Non-Obstructive Hypertrophic Cardiomyopathy (nHCM)

A Pilot Study of the Utility of 3D Printed Masks for ALS Subjects